Development of new effective therapies for rare diseases

Last updated: 16.7.2025
Grant

The 'Development of new effective therapies for rare diseases' program, under Horizon Europe, aims to address the urgent unmet medical needs in rare diseases by fostering the development of novel therapeutic interventions. It specifically targets groups of rare diseases with commonalities, moving beyond single-disease approaches. The program encourages multidisciplinary collaborations and the involvement of patient representatives to accelerate the translation of research into accessible treatments.

Who is Funded

This program supports a broad range of entities and collaborations across various geographical areas, all united by the common goal of advancing therapies for rare diseases. It aims to significantly reduce the burden of diseases globally and strengthen healthcare systems.

What is Funded

This program provides funding for a diverse range of research and innovation activities across critical health sectors, focusing on advancing therapeutic solutions from early development to market uptake.

Type and Scope of Funding

The financial support provided through this program is in the form of grants, with a significant maximum funding amount per project to foster impactful research and development.

Conditions and Requirements

Applicants and beneficiaries must adhere to a series of specific conditions and requirements throughout the application and project implementation phases, encompassing administrative, collaborative, and regulatory stipulations.

Application Procedure

The application process for this program is structured in two stages, involving detailed evaluation criteria and specific timelines for submission and notification.

The program is firmly rooted in established European Union legal frameworks and policies, ensuring transparency and proper governance.

Similar Programs

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Funding Overview

Funding Status

Funding Status:

Closed

Maximum Amount

Maximum Amount:

8,000,000 €

Allocated Budget

Allocated Budget:

60,000,000 EUR

Award Channel

Award Channel:

Framework Programme Call

Region

Region:

European Union Member States and Associated Countries. Legal entities established in the United States of America are also eligible for funding. Other non-EU/non-Associated countries may also be eligible as specified in the Horizon Europe Programme Guide.

Sectors

Sectors:

Healthcare, Medical Technology, Pharmaceutical Industry, Research and Development

Beneficiaries

Beneficiaries:

Patients with rare diseases, Healthcare providers

Application Type

Application Type:

Consortium Required

Funding Stages

Funding Stages:

Applied Research, Experimental Development, Prototyping, Pilot Testing, Product Development, Market Introduction, Commercialization

Funding Provider

Program Level:

European Union

Funding Body:

European Commission

Managed By:

Unknown

Additional Partners:

Joint Research Centre (JRC)

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